Mutation

Understanding Synaptic Dysfunction and Extracellular Matrix Dysregulation in Dopaminergic Neurons of Sporadic and E326K-GBA1 Parkinson’s Disease Patients: Insights from npj...

Repotrectinib, a promising targeted therapy, has shown significant tumor reduction in patients with ROS1-positive non-small cell lung cancer (NSCLC). This...

FDA Expedites Development of RNA Exon Editor for Stargardt Disease in Clinical Trials Stargardt disease, also known as Stargardt macular...

EMA’s CHMP Declines Renewal of Translarna and Rejects Nezglyal and Syfovre as New Medicines The European Medicines Agency’s (EMA) Committee...

Title: Pioneering Gene Therapy Enables a Deaf Child to Hear for the First Time Introduction: In a groundbreaking achievement, scientists...

Gene Therapy Offers New Hope for Children with Congenital Deafness, According to Drugs.com MedNews Deafness is a condition that affects...

Title: Investigating the Correlation between Type 1 CALR Mutation Allele Frequency and CD34/CXCR4 Expression in Myelofibrosis-Type Megakaryocyte Dysplasia: Unraveling a...

Machine learning techniques have revolutionized various industries, including data management and analysis. One area where machine learning has shown significant...

The field of gene editing has reached a significant milestone with the recent approval of CRISPR therapy by the U.S....

Title: FDA Approves Sickle Cell Drug for Treatment of Additional Blood Disorder – Comprehensive Update from Drugs.com MedNews Introduction In...

The U.S. Food and Drug Administration (FDA) has recently expanded its approval of Vertex Pharmaceuticals’ CRISPR-based medicine for the treatment...

New Developments in NSCLC Treatment: Strategies to Overcome Osimertinib Resistance Non-small cell lung cancer (NSCLC) is the most common type...

Key Research Findings from MSK, December 29, 2023 As we approach the end of another year, it is essential to...

Insilico Medicine, a leading artificial intelligence (AI) company focused on drug discovery and development, has been making significant strides in...